P014: First-in-human phase 1/2 trial of intravenous FBX-101 with cord blood transplantation increases GALC, brain and motor development in infantile Krabbe
Maria Escolar,
Mark Vander Lugt,
Michele Poe,
Melissa Greco,
Keith Werling,
Erandi De Silva,
Juan Ruiz,
Paul Szabolcs
Affiliations
Maria Escolar
Forge Biologics
Mark Vander Lugt
University of Michigan, C.S. Mott Children's Hospital
Michele Poe
Forge Biologics
Melissa Greco
University of Pittsburgh, UPMC Children's Hospital
Keith Werling
University of Pittsburgh, UPMC Children's Hospital
Erandi De Silva
Forge Biologics
Juan Ruiz
Forge Biologics
Paul Szabolcs
University of Pittsburgh, UPMC Children's Hospital