CRISPR-Cas9-directed gene therapy for spinocerebellar ataxia type 1

• Mihai Miclăuș,
• Gabriel Balmus

Affiliations

Mihai Miclăuș

UK Dementia Research Institute at the University of Cambridge, Cambridge CB2 0AH, UK; Department of Molecular Neuroscience, Transylvanian Institute of Neuroscience, 400191 Cluj-Napoca, Romania

Gabriel Balmus

UK Dementia Research Institute at the University of Cambridge, Cambridge CB2 0AH, UK; Department of Clinical Neurosciences, University of Cambridge, Cambridge Biomedical Campus, Cambridge CB2 0AH, UK; Department of Molecular Neuroscience, Transylvanian Institute of Neuroscience, 400191 Cluj-Napoca, Romania; Corresponding author: Gabriel Balmus, UK Dementia Research Institute at the University of Cambridge and Department of Clinical Neurosciences, University of Cambridge, Cambridge Biomedical Campus, Cambridge CB2 0AH, UK.