The CFTR Corrector, VX-809 (Lumacaftor), Rescues ABCA4 Trafficking Mutants: a Potential Treatment for Stargardt Disease

• Qiangni Liu,
• Inna Sabirzhanova,
• Emily Anne Smith Bergbower,
• Murali Yanda,
• William G. Guggino,
• Liudmila Cebotaru

Affiliations

Qiangni Liu

Division of Gastroenterology and Hepatology, Departments of Medicine, Johns Hopkins University, Baltimore, MD, USA

Inna Sabirzhanova

Division of Gastroenterology and Hepatology, Departments of Medicine, Johns Hopkins University, Baltimore, MD, USA

Emily Anne Smith Bergbower

Division of Gastroenterology and Hepatology, Departments of Medicine, Johns Hopkins University, Baltimore, MD, USA

Murali Yanda

Division of Gastroenterology and Hepatology, Departments of Medicine, Johns Hopkins University, Baltimore, MD, USA

William G. Guggino

Division of Gastroenterology and Hepatology, Departments of Medicine, Johns Hopkins University, Baltimore, MD, USA

Liudmila Cebotaru

Division of Gastroenterology and Hepatology, Departments of Medicine, Johns Hopkins University, Baltimore, MD, USA