Stem Cell Research (Dec 2020)

Generation of iPSC lines from two patients affected by febrile seizure due to inherited missense mutation in SCN1A gene

  • Stefania Scalise,
  • Luana Scaramuzzino,
  • Valeria Lucchino,
  • Claudia Esposito,
  • Paola Malatesta,
  • Katia Grillone,
  • Nicola Perrotti,
  • Giovanni Cuda,
  • Elvira Immacolata Parrotta

Journal volume & issue
Vol. 49
p. 102083

Abstract

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Here, we described the generation of human induced pluripotent stem cell lines (hiPSCs) from fibroblasts isolated by punch biopsies of two siblings carrying inherited mutation (c.434 T > C) in the SCN1A gene, encoding for the neuronal voltage gated sodium channel NaV1.1. The mutation leads to the substitution of a highly conserved methionine with a threonine (M145T) in the protein sequence, leading to infant febrile seizures (FS). The older brother, affected by complex FS, also developed temporal lobe epilepsy (TLE) during adolescence.