P094: Clinical and MRI correlations in GM1 patients: Finding biomarkers to predict treatment response with gene therapy*

• Maria T. Acosta,
• Zeynep Vardar,
• Precilla D'Souza,
• Jean Johnston,
• Anna Kuhn,
• Audrey Thurm,
• Cristan Farmer,
• Mohammed Shazeeb,
• Cynthia Tifft

Affiliations

Maria T. Acosta

Office of the Clinical Director, National Human Genome Research Institute, National Institutes of Health, Bethesda, MD

Zeynep Vardar

Department of Radiology, University of Massachusetts Chan Medical School, Worcester, MA

Precilla D'Souza

Office of the Clinical Director, National Human Genome Research Institute, National Institutes of Health, Bethesda, MD

Jean Johnston

Office of the Clinical Director, National Human Genome Research Institute, National Institutes of Health, Bethesda, MD

Anna Kuhn

Department of Radiology, University of Massachusetts Chan Medical School, Worcester, MA

Audrey Thurm

National Institute of Mental Health, National Institutes of Health, Bethesda, MD

Cristan Farmer

National Institute of Mental Health, National Institutes of Health, Bethesda, MD

Mohammed Shazeeb

Department of Radiology, University of Massachusetts Chan Medical School, Worcester, MA

Cynthia Tifft

Office of the Clinical Director, National Human Genome Research Institute, National Institutes of Health, Bethesda, MD