Progress in gene therapy

Abstract

Recent progress in gene therapy, current status of investigations in this area of experimental medicine are reviewed. Much attention is given to gene-therapeutic approaches the efficacy of which is proved in clinical trials.

Keywords

• review
• gene therapy
• gene delivery
• transgene
• vectors
• clinical trials
• congenital immunodeficiencies
• severe combined immunodeficiency
• leber's amavrosis
• adrenoleukodystrophy