A novel porcine model of CLN3 Batten disease recapitulates clinical phenotypes

• Vicki J. Swier,
• Katherine A. White,
• Tyler B. Johnson,
• Xiaojun Wang,
• Jimin Han,
• David A. Pearce,
• Ruchira Singh,
• Arlene V. Drack,
• Wanda Pfeifer,
• Christopher S. Rogers,
• Jon J. Brudvig,
• Jill M. Weimer

Affiliations

Vicki J. Swier

Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD 57104, USA

Katherine A. White

Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD 57104, USA

Tyler B. Johnson

Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD 57104, USA

Xiaojun Wang

Precigen Exemplar, Coralville, IA 52241, USA

Jimin Han

Department of Ophthalmology, Center for Visual Science, University of Rochester Medical Center, Rochester, NY 14642, USA

David A. Pearce

Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD 57104, USA

Ruchira Singh

Department of Ophthalmology, Center for Visual Science, University of Rochester Medical Center, Rochester, NY 14642, USA

Arlene V. Drack

Department of Ophthalmology and Visual Sciences, University of Iowa, Iowa City, IA 52242, USA

Wanda Pfeifer

Department of Ophthalmology and Visual Sciences, University of Iowa, Iowa City, IA 52242, USA

Christopher S. Rogers

Precigen Exemplar, Coralville, IA 52241, USA

Jon J. Brudvig

Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD 57104, USA

Jill M. Weimer

Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD 57104, USA