HemaSphere
(Jun 2022)
P1547: ACTIVATE-KIDS: MITAPIVAT IN CHILDREN WITH PYRUVATE KINASE DEFICIENCY WHO ARE NOT REGULARLY TRANSFUSED
- R. F. Grace,
- P. D. Tyler,
- M. Little,
- P. A. Kosinski,
- V. Beynon
Affiliations
- R. F. Grace
- 1 Dana-Farber/Boston Children’s Cancer and Blood Disorders Center, Harvard Medical School, Boston, MA
- P. D. Tyler
- 2 Agios Pharmaceuticals, Inc., Cambridge, MA, United States of America
- M. Little
- 2 Agios Pharmaceuticals, Inc., Cambridge, MA, United States of America
- P. A. Kosinski
- 2 Agios Pharmaceuticals, Inc., Cambridge, MA, United States of America
- V. Beynon
- 2 Agios Pharmaceuticals, Inc., Cambridge, MA, United States of America
- DOI
-
https://doi.org/10.1097/01.HS9.0000849044.32404.85
- Journal volume & issue
-
Vol. 6
pp.
1428
– 1429
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