Orphanet Journal of Rare Diseases (Jun 2021)
Correction to: Clinical disease progression and biomarkers in Niemann–Pick disease type C: a prospective cohort study
- Eugen Mengel,
- Bruno Bembi,
- Mireia del Toro,
- Federica Deodato,
- Matthias Gautschi,
- Stephanie Grunewald,
- Sabine Grønborg,
- Bénédicte Héron,
- Esther M. Maier,
- Agathe Roubertie,
- Saikat Santra,
- Anna Tylki-Szymanska,
- Simon Day,
- Tara Symonds,
- Stacie Hudgens,
- Marc C. Patterson,
- Christina Guldberg,
- Linda Ingemann,
- Nikolaj H. T. Petersen,
- Thomas Kirkegaard,
- Christine í Dali
Affiliations
- Eugen Mengel
- SphinCS GmbH, Institute of Clinical Science for LSD
- Bruno Bembi
- Regional Coordinator Centre for Rare Diseases, Academic Hospital Santa Maria Della Misericordia
- Mireia del Toro
- Vall D’Hebron University Hospital
- Federica Deodato
- Ospedale Pediatrico Bambino Gesù, IRCCS
- Matthias Gautschi
- Inselspital, University Hospital of Bern
- Stephanie Grunewald
- Metabolic Department, Great Ormond Street Hospital NHS Foundation Trust, Institute for Child Health, NIHR Biomedical Research Centre UCL
- Sabine Grønborg
- Centre for Inherited Metabolic Diseases, Copenhagen University Hospital (Rigshospitalet)
- Bénédicte Héron
- Reference Centre for Lysosomal Disease, Trousseau University Hospital
- Esther M. Maier
- Dr. Von Hauner Children’s Hospital, University of Munich
- Agathe Roubertie
- Institute of Neurosciences, University Hospital of Montpellier
- Saikat Santra
- Birmingham Children’s Hospital
- Anna Tylki-Szymanska
- Children’s Memorial Health Institute
- Simon Day
- Clinical Trials Consulting and Training Limited
- Tara Symonds
- Clinical Outcomes Solutions Limited
- Stacie Hudgens
- Clinical Outcomes Solutions Inc
- Marc C. Patterson
- Mayo Clinic Children’s Center
- Christina Guldberg
- Orphazyme A/S
- Linda Ingemann
- Orphazyme A/S
- Nikolaj H. T. Petersen
- Orphazyme A/S
- Thomas Kirkegaard
- Orphazyme A/S
- Christine í Dali
- Orphazyme A/S
- DOI
- https://doi.org/10.1186/s13023-021-01855-9
- Journal volume & issue
-
Vol. 16,
no. 1
pp. 1 – 3
Abstract
An amendment to this paper has been published and can be accessed via the original article.
