P012: Pegtibatinase, an investigational enzyme replacement therapy for the treatment of classical homocystinuria: Latest findings from the COMPOSE phase 1/2 trial
Can Ficicioglu,
Jaya Ganesh,
Wendy Smith,
Melissa Lah,
David Kudrow,
Jalé Güner,
Sharon McDermott,
Sagar Vaidya,
Liz Wilkening,
Janet Thomas,
Harvey Levy
Affiliations
Can Ficicioglu
Children’s Hospital of Philadelphia, University of Pennsylvania, Perelman School of Medicine
Jaya Ganesh
Icahn School of Medicine at Mount Sinai
Wendy Smith
Maine Medical Center
Melissa Lah
Indiana University School of Medicine
David Kudrow
Science 37
Jalé Güner
Travere Therapeutics Inc
Sharon McDermott
Travere Therapeutics Inc
Sagar Vaidya
Travere Therapeutics Inc
Liz Wilkening
Travere Therapeutics Inc
Janet Thomas
University of Colorado School of Medicine
Harvey Levy
Boston Children’s Hospital, Harvard Medical School