Genetics in Medicine Open (Jan 2024)

P012: Pegtibatinase, an investigational enzyme replacement therapy for the treatment of classical homocystinuria: Latest findings from the COMPOSE phase 1/2 trial

  • Can Ficicioglu,
  • Jaya Ganesh,
  • Wendy Smith,
  • Melissa Lah,
  • David Kudrow,
  • Jalé Güner,
  • Sharon McDermott,
  • Sagar Vaidya,
  • Liz Wilkening,
  • Janet Thomas,
  • Harvey Levy

Journal volume & issue
Vol. 2
p. 100889

Abstract

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