O19: Antisense oligonucleotide targeting a linked-SNP provides allele-specific and effective knockdown to a dominant negative SPTAN1 pathogenic variant
Christiana Wang,
Shenglan Li,
Sen Zhao,
Jefferson Sinson,
Nhi Ho,
Blake Vuocolo,
Gary Clark,
Sandesh Nagamani,
Pengfei Liu
Affiliations
Christiana Wang
Baylor College of Medicine
Shenglan Li
Baylor College of Medicine
Sen Zhao
Baylor College of Medicine
Jefferson Sinson
Baylor College of Medicine
Nhi Ho
Baylor College of Medicine
Blake Vuocolo
Baylor College of Medicine
Gary Clark
Baylor College of Medicine, Texas Children's Hospital
Sandesh Nagamani
Baylor College of Medicine, Texas Children's Hospital
