Genetics in Medicine Open (Jan 2023)
O19: Integrated analyses of data from clinical trials of delandistrogene moxeparvovec gene therapy in DMD*
- Erin O’Rourke,
- Crystal Proud,
- Craig Zaidman,
- Perry B. Shieh,
- Craig McDonald,
- John W. Day,
- Stefanie Mason,
- Maitea Guridi,
- Lixin Han,
- Lixi Yu,
- Carol Reid,
- Eddie Darton,
- Christoph Wandel,
- James Richardson,
- Jyoti Malhotra,
- Teji Singh,
- Louise Rodino-Klapac,
- Jerry Mendell
Affiliations
- Erin O’Rourke
- Sarepta Therapeutics, Inc.
- Crystal Proud
- Children’s Hospital of the King’s Daughters
- Craig Zaidman
- Department of Neurology, WUSTL
- Perry B. Shieh
- UCLA Medical Center
- Craig McDonald
- UC Davis Health
- John W. Day
- Department of Neurology, Stanford University
- Stefanie Mason
- Sarepta Therapeutics, Inc.
- Maitea Guridi
- F. Hoffmann-La Roche Ltd
- Lixin Han
- Sarepta Therapeutics, Inc.
- Lixi Yu
- Sarepta Therapeutics, Inc.
- Carol Reid
- Roche Products Ltd
- Eddie Darton
- Sarepta Therapeutics, Inc.
- Christoph Wandel
- F. Hoffmann-La Roche Ltd
- James Richardson
- Sarepta Therapeutics, Inc.
- Jyoti Malhotra
- Sarepta Therapeutics, Inc.
- Teji Singh
- Sarepta Therapeutics, Inc.
- Louise Rodino-Klapac
- Sarepta Therapeutics, Inc.
- Jerry Mendell
- Center for Gene Therapy, Nationwide Children’s Hospital
- Journal volume & issue
-
Vol. 1,
no. 1
p. 100115