Molecular Therapy: Nucleic Acids (Jan 2014)

What Can We Learn From Clinical Trials of Exon Skipping for DMD?

  • Qi-long Lu,
  • Sebahattin Cirak,
  • Terence Partridge

DOI
https://doi.org/10.1038/mtna.2014.6
Journal volume & issue
Vol. 3, no. C

Abstract

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