Olipudase alfa approved for pediatric and adult patients with acid sphingomyelinase deficiency (ASMD): A therapeutics bulletin of the American College of Medical Genetics and Genomics (ACMG)
Monica Penon-Portmann,
Sheri A. Poskanzer,
Jaya Ganesh,
Irene Chang
Affiliations
Monica Penon-Portmann
Division of Genetic Medicine, Department of Pediatrics, University of Washington, Seattle, WA
Sheri A. Poskanzer
St. Luke’s Health System, Boise, ID
Jaya Ganesh
Department of Genetics and Genomic Sciences, Mount Sinai, New York, NY
Irene Chang
Division of Genetic Medicine, Department of Pediatrics, University of Washington, Seattle, WA
