Genetics in Medicine Open (Jan 2023)
O22: A randomized controlled trial of vosoritide in infants and toddlers with achondroplasia*
- Carlos Bacino,
- Ravi Savarirayan,
- William Wilcox,
- Paul Harmatz,
- John Phillips,
- Lynda Polgreen,
- Louise Tofts,
- Keiichi Ozono,
- Paul Arundel,
- Melita Irving,
- Donald Basel,
- Michael Bober,
- Joel Charrow,
- Hiroshi Mochizuki,
- Yumiko Kotani,
- Howard Saal,
- George Jeha,
- Lynn Han,
- Elena Fisheleva,
- Alice Huntsman-Labed,
- Jonathan Day
Affiliations
- Carlos Bacino
- Baylor College of Medicine, Houston, TX
- Ravi Savarirayan
- Murdoch Children’s Research Institute, Royal Children’s Hospital, and University of Melbourne, Parkville, Victoria, Australia
- William Wilcox
- Emory University, Atlanta, GA
- Paul Harmatz
- UCSF Benioff Children’s Hospital Oakland, Oakland, CA
- John Phillips
- Vanderbilt University Medical Center, Nashville, TN
- Lynda Polgreen
- Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center, Torrance, CA
- Louise Tofts
- Kids Rehab, The Children's Hospital at Westmead, Westmead, New South Wales, Australia
- Keiichi Ozono
- Osaka University Hospital, Osaka, Japan
- Paul Arundel
- Sheffield Children's NHS Foundation Trust, Sheffield Children's Hospital, Sheffield, UK
- Melita Irving
- Guy’s and St. Thomas’ NHS Foundation Trust, Evelina Children's Hospital, London, UK
- Donald Basel
- Medical College of Wisconsin, Milwaukee, WI
- Michael Bober
- Nemours/Alfred I. du Pont Hospital for Children, Wilmington, DE
- Joel Charrow
- Ann and Robert H. Lurie Children’s Hospital of Chicago, Chicago, IL
- Hiroshi Mochizuki
- Saitama Children’s Hospital, Saitama, Japan
- Yumiko Kotani
- Tokushima University Hospital, Tokushima, Japan
- Howard Saal
- Cincinnati Children’s Hospital Medical Center, University of Cincinnati College of Medicine, Cincinnati, OH
- George Jeha
- BioMarin Pharmaceutical Inc., Novato, CA
- Lynn Han
- BioMarin Pharmaceutical Inc., Novato, CA
- Elena Fisheleva
- BioMarin (U.K.) Limited, London, UK
- Alice Huntsman-Labed
- BioMarin (U.K.) Limited, London, UK
- Jonathan Day
- BioMarin (U.K.) Limited, London, UK
- Journal volume & issue
-
Vol. 1,
no. 1
p. 100118
