Editorial: New Therapeutic Options for Rare Diseases

• Sascha Meyer,
• E. Ann Yeh,
• Jürgen Brunner,
• Jürgen Brunner,
• Oliver Semler,
• Andrea Gropman

Affiliations

Sascha Meyer

Department General Pediatrics, Neonatology, and Neuropediatrics, University Hospital of Saarland, Homburg, Germany

E. Ann Yeh

Division of Neurology, Department of Pediatrics, Neurosciences and Mental Health, SickKids Research Institute, Hospital for Sick Children, University of Toronto, Toronto, ON, Canada

Jürgen Brunner

Department of Pediatrics, Innsbruck Medical University, Innsbruck, Austria

Jürgen Brunner

Danube Private University, Krems, Austria

Oliver Semler

Department of Pediatrics, Faculty of Medicine and University Hospital Cologne, University of Cologne, Cologne, Germany

Andrea Gropman

Neurogenetics and Neurodevelopmental Pediatrics, George Washington School of Medicine and Health Sciences, Washington, DC, United States