Genetics in Medicine Open (Jan 2024)

P449: Fidrisertib (IPN60130) for the treatment of fibrodysplasia ossificans progressiva: Methodology of the randomized, double-blind, placebo-controlled phase II FALKON trial

  • Negar Karimian,
  • Caroline Brard,
  • Jeanna Cooper,
  • Fei Shih

Journal volume & issue
Vol. 2
p. 101343

Abstract

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