P1543: MITAPIVAT DECREASES THE NEED FOR TRANSFUSIONS SECONDARY TO POORLY TOLERATED ANEMIA AND ACUTE EVENTS COMPARED TO PLACEBO IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY WHO ARE NOT REGULARLY TRANSFUSED

• H. Al-Samkari,
• J. Morales-Arias,
• R. Xu,
• V. Beynon,
• R. F. Grace

Affiliations

H. Al-Samkari

1 Division of Hematology, Massachusetts General Hospital, Harvard Medical School, Boston

J. Morales-Arias

2 Agios Pharmaceuticals, Inc., Cambridge

R. Xu

2 Agios Pharmaceuticals, Inc., Cambridge

V. Beynon

2 Agios Pharmaceuticals, Inc., Cambridge

R. F. Grace

3 Dana-Farber/Boston Children’s Cancer and Blood Disorders Center, Boston, United States of America