Molecular Therapy: Nucleic Acids (Jun 2023)

AAV-vectored base editor trans-splicing delivers dystrophin repair

Zhen Li,
Manuel A.F.V. Gonçalves

Affiliations

Zhen Li: Leiden University Medical Centre, Department of Cell and Chemical Biology, Einthovenweg 20, 2333 ZC Leiden, the Netherlands
Manuel A.F.V. Gonçalves: Leiden University Medical Centre, Department of Cell and Chemical Biology, Einthovenweg 20, 2333 ZC Leiden, the Netherlands; Corresponding author: Manuel A.F.V. Gonçalves, Leiden University Medical Centre, Department of Cell and Chemical Biology, Einthovenweg 20, 2333 ZC Leiden, the Netherlands.

Journal volume & issue: Vol. 32
pp. 900 – 902

Abstract

No abstracts available.

Published in Molecular Therapy: Nucleic Acids

ISSN: 2162-2531 (Online)
Publisher: Elsevier
Country of publisher: United States
LCC subjects: Medicine: Therapeutics. Pharmacology
Website: https://www.cell.com/molecular-therapy-family/nucleic-acids/latest-content

About the journal