Circulating neurofilaments to track dorsal root ganglion toxicity risks with AAV-mediated gene therapy

• Michelle A. Farrar,
• Ewout Groen,
• Christiano Alves

Affiliations

Michelle A. Farrar

Department of Neurology, Sydney Children’s Hospital Network, Level 8, Bright Alliance Building, Avoca Street, Randwick, NSW 2031, Australia; Discipline of Paediatrics and Child Health, School of Clinical Medicine, UNSW Medicine and Health, UNSW Sydney, Kensington, NSW 2052, Australia; Corresponding author Michelle A. Farrar, Level 8, Bright Alliance Building, Avoca Street, Department of Neurology, Sydney Children’s Hospital Network, Randwick, NSW 2031, Australia.

Ewout Groen

Department of Neurology, UMC Utrecht Brain Center, 3584 CX Utrecht, the Netherlands

Christiano Alves

Department of Neurology, Massachusetts General Hospital, Harvard Medical School, Boston, MA 02114, USA; Center for Genomic Medicine, Simches Research Center, Massachusetts General Hospital, Boston, MA 02114, USA