Expression and function of four AAV-based constructs for dystrophin restoration in the mdx mouse model of Duchenne muscular dystrophy

• Rachael A. Potter,
• Danielle A. Griffin,
• Kristin N. Heller,
• Jerry R. Mendell,
• Louise R. Rodino-Klapac

Affiliations

Rachael A. Potter

Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, OH 43205, USA

Danielle A. Griffin

Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, OH 43205, USA

Kristin N. Heller

Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, OH 43205, USA

Jerry R. Mendell

Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, OH 43205, USA

Louise R. Rodino-Klapac

Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, OH 43205, USA