Translational Neurodegeneration (Dec 2024)
Recombinant SMN protein synergizes with spinal muscular atrophy therapy to counteract pathological motor neuron phenotypes
- Liliana Brambilla,
- Chiara F. Valori,
- Giulia Guidotti,
- Francesca Martorana,
- Claudia Sulmona,
- Lisa Benedetta De Martini,
- Anselmo Canciani,
- Marco Fumagalli,
- Francesca Talpo,
- Gerardo Biella,
- Elisa Di Pasquale,
- Claudio Iacobucci,
- Federico Forneris,
- Haiyan Zhou,
- Daniela Rossi
Affiliations
- Liliana Brambilla
- Laboratory for Research on Neurodegenerative Disorders, Istituti Clinici Scientifici Maugeri IRCCS
- Chiara F. Valori
- Laboratory for Research on Neurodegenerative Disorders, Istituti Clinici Scientifici Maugeri IRCCS
- Giulia Guidotti
- Laboratory for Research on Neurodegenerative Disorders, Istituti Clinici Scientifici Maugeri IRCCS
- Francesca Martorana
- Laboratory for Research on Neurodegenerative Disorders, Istituti Clinici Scientifici Maugeri IRCCS
- Claudia Sulmona
- Laboratory for Research on Neurodegenerative Disorders, Istituti Clinici Scientifici Maugeri IRCCS
- Lisa Benedetta De Martini
- Laboratory for Research on Neurodegenerative Disorders, Istituti Clinici Scientifici Maugeri IRCCS
- Anselmo Canciani
- The Armenise-Harvard Laboratory of Structural Biology, Department of Biology and Biotechnology, University of Pavia
- Marco Fumagalli
- The Armenise-Harvard Laboratory of Structural Biology, Department of Biology and Biotechnology, University of Pavia
- Francesca Talpo
- Department of Biology and Biotechnology, University of Pavia
- Gerardo Biella
- Department of Biology and Biotechnology, University of Pavia
- Elisa Di Pasquale
- Humanitas Cardio Center, IRCCS Humanitas Research Hospital
- Claudio Iacobucci
- Department of Physical and Chemical Sciences, University of L’Aquila
- Federico Forneris
- The Armenise-Harvard Laboratory of Structural Biology, Department of Biology and Biotechnology, University of Pavia
- Haiyan Zhou
- Dubowitz Neuromuscular Centre and National Institute for Health Research, Great Ormond Street Institute of Child Health, Biomedical Research Centre, University College London
- Daniela Rossi
- Laboratory for Research on Neurodegenerative Disorders, Istituti Clinici Scientifici Maugeri IRCCS
- DOI
- https://doi.org/10.1186/s40035-024-00455-4
- Journal volume & issue
-
Vol. 13,
no. 1
pp. 1 – 5
Abstract
No abstracts available.