Translational Neurodegeneration (Dec 2024)

Recombinant SMN protein synergizes with spinal muscular atrophy therapy to counteract pathological motor neuron phenotypes

  • Liliana Brambilla,
  • Chiara F. Valori,
  • Giulia Guidotti,
  • Francesca Martorana,
  • Claudia Sulmona,
  • Lisa Benedetta De Martini,
  • Anselmo Canciani,
  • Marco Fumagalli,
  • Francesca Talpo,
  • Gerardo Biella,
  • Elisa Di Pasquale,
  • Claudio Iacobucci,
  • Federico Forneris,
  • Haiyan Zhou,
  • Daniela Rossi

DOI
https://doi.org/10.1186/s40035-024-00455-4
Journal volume & issue
Vol. 13, no. 1
pp. 1 – 5

Abstract

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