Neural Regeneration Research (Jul 2025)

Gene therapy for spinal muscular atrophy: perspectives on the possibility of optimizing SMN1 delivery to correct all neurological and systemic perturbations

  • Sharon J. Brown,
  • Rafael J. Yáñez-Muñoz,
  • Heidi R. Fuller

DOI
https://doi.org/10.4103/NRR.NRR-D-24-00504
Journal volume & issue
Vol. 20, no. 7
pp. 2011 – 2012

Abstract

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