From the voice of patients and caregivers: Burden of illness in infantile onset ABCC6 and ENPP1 deficiency (GACI and ARHR2)

• Christine O'Brien,
• Beth Leiro,
• Gus Khursigara,
• Catherine Nester,
• Pedro Huertas

Affiliations

Christine O'Brien

GACI Global, Co-President, Boston, United States

Beth Leiro

Origin Biosciences, N/a, Chapel Hill, United States

Gus Khursigara

Inozyme Pharma- Inc., Medical Affairs, Boston, United States

Catherine Nester

Inozyme Pharma- Inc., Medical Affairs, Boston, United States; Corresponding author.

Pedro Huertas

Inozyme Pharma- Inc., Medical Affairs, Boston, United States