P1588: LONG-TERM REAL-WORLD EFFECTIVENESS OF ELIGLUSTAT IN TREATMENT-NAÏVE AND SWITCH PATIENTS ENROLLED IN THE INTERNATIONAL COLLABORATIVE GAUCHER GROUP (ICGG) GAUCHER REGISTRY

• Pramod Mistry,
• Manisha Balwani,
• Joel Charrow,
• Jeremy Lorber,
• Claus Niederau,
• Jenny Carwile,
• Sefika Uslu,
• Priya S. Kishnani

Affiliations

Pramod Mistry

1 Yale University School of Medicine, New Haven, United States

Manisha Balwani

2 Icahn School of Medicine at Mount Sinai, Department of Genetics and Genomic Sciences, New York, United States

Joel Charrow

3 Ann & Robert H Lurie Children’s Hospital of Chicago, Chicago, United States

Jeremy Lorber

4 Cedars-Sinai Medical Center, Los Angeles, California, United States

Claus Niederau

5 Katholisches Klinikum Oberhausen, Department of Medicine, Oberhausen, Germany

Jenny Carwile

6 Sanofi, Rare Disease, Epidemiology and Biostatistics, Cambridge, MA, United States

Sefika Uslu

7 Sanofi, Rare Hematology, Cambridge, MA, United States

Priya S. Kishnani

8 Duke University, Division of Medical Genetics, Department of Pediatrics, Durham, North Carolina, United States