Strengthening health systems for access to gene therapy in rare genetic disorders

• Sonal Bhatia,
• Yann Le Cam,
• Juan Carrion,
• Lauren Diamond,
• Paul Fennessy,
• Safiyya Gassman,
• Felix Gutzwiller,
• Stephen Kagan,
• Diana Pankevich,
• Jennifer Young Maloney,
• Nitin Mahadev,
• Martin Schulz,
• Durhane Wong-Rieger,
• Paolo Morgese

Affiliations

Sonal Bhatia

Pfizer, Inc., New York, NY, USA

Yann Le Cam

EURORDIS, Paris, France

Juan Carrion

Aliber, Totana, Spain

Lauren Diamond

Pfizer, Inc., New York, NY, USA

Paul Fennessy

Paul Fennessy Advisory, Melbourne, VIC, Australia

Safiyya Gassman

Pfizer, Inc., New York, NY, USA

Felix Gutzwiller

University of Zurich, Zurich, Switzerland

Stephen Kagan

Pfizer, Inc., New York, NY, USA

Diana Pankevich

Pfizer, Inc., New York, NY, USA

Jennifer Young Maloney

Pfizer, Inc., New York, NY, USA

Nitin Mahadev

Pfizer, Inc., New York, NY, USA

Martin Schulz

Pfizer, Inc., New York, NY, USA; Corresponding author: Martin Schulz, Pfizer, Inc., New York, NY, USA.

Durhane Wong-Rieger

Canadian Organization for Rare Disorders, Toronto, ON, Canada

Paolo Morgese

Alliance for Regenerative Medicine, Brussels, Belgium