PB2043: CLINICAL EFFECTIVENESS, TREATMENT USE, SATISFACTION AND IMPACT ON QUALITY-OF-LIFE OF PEGCETACOPLAN TREATMENT FOR PATIENTS WITH PAROXYSMAL NOCTURNAL HAEMOGLOBINURIA (PNH).
Koo Wilson,
Carly Rich,
Zalmai Hakimi,
Jesse Fishman,
Jennifer Mellor,
Lucy Earl,
Yasmin Taylor,
Alice Simons,
Joe Conyers,
Alexander Röth
Affiliations
Koo Wilson
1 Swedish Orphan Biovitrum AB (Sobi™)
Carly Rich
1 Swedish Orphan Biovitrum AB (Sobi™)
Zalmai Hakimi
1 Swedish Orphan Biovitrum AB (Sobi™)
Jesse Fishman
2 Apellis Pharmaceuticals, Inc.
Jennifer Mellor
3 Adelphi Real World, Manchester
Lucy Earl
3 Adelphi Real World, Manchester
Yasmin Taylor
3 Adelphi Real World, Manchester
Alice Simons
3 Adelphi Real World, Manchester
Joe Conyers
3 Adelphi Real World, Manchester
Alexander Röth
4 University Hospital Essen, Department of Hematology and Stem Cell Transplantation