P1546: ACTIVATE-KIDST: MITAPIVAT IN CHILDREN WITH PYRUVATE KINASE DEFICIENCY WHO ARE REGULARLY TRANSFUSED

• R. F. Grace,
• P. D. Tyler,
• M. Little,
• P. A. Kosinski,
• V. Beynon

Affiliations

R. F. Grace

1 Dana-Farber/Boston Children’s Cancer and Blood Disorders Center, Harvard Medical School, Boston

P. D. Tyler

2 Agios Pharmaceuticals, Inc., Cambridge, United States of America

M. Little

2 Agios Pharmaceuticals, Inc., Cambridge, United States of America

P. A. Kosinski

2 Agios Pharmaceuticals, Inc., Cambridge, United States of America

V. Beynon

2 Agios Pharmaceuticals, Inc., Cambridge, United States of America