Long-term dystrophin restoration supports development of splice correction therapy for DMD patients with exon 2 duplications

• Thomas C. Roberts

Affiliations

Thomas C. Roberts

Department of Paediatrics, University of Oxford, Oxford OX3 7TY, UK; Institute of Developmental and Regenerative Medicine, University of Oxford, IMS-Tetsuya Nakamura Building, Oxford OX3 7TY, UK; MDUK Oxford Neuromuscular Centre, Oxford OX3 7TY, UK; Corresponding author: Thomas C. Roberts, Institute of Developmental and Regenerative Medicine, University of Oxford, IMS-Tetsuya Nakamura Building, Oxford OX3 7TY, UK.