HemaSphere (Jun 2022)

P826: FACTOR D INHIBITION WITH ORAL BCX9930 LEADS TO SUSTAINED CONTROL OF HEMOLYSIS AND SYMPTOMS OVER 48 WEEKS IN SUBJECTS WITH PAROXYSMAL NOCTURNAL HEMOGLOBINURIA INADEQUATELY CONTROLLED ON C5 INHIBITORS

  • A. Kulasekararaj,
  • W. Füreder,
  • A. McDonald,
  • J. L. R. Malherbe,
  • S. Gandhi,
  • D. Collins,
  • M. Cornpropst,
  • S. Dobo,
  • M. K. Farmer,
  • D. Kargl,
  • W. Sheridan,
  • M. Griffin,
  • A. Risitano

DOI
https://doi.org/10.1097/01.HS9.0000846188.51290.75
Journal volume & issue
Vol. 6
pp. 720 – 721

Abstract

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