P176: Real world experience of velaglucerase alfa in children under 4 years of age with Gaucher disease: A retrospective/prospective study

• Ozlem Goker-Alpan,
• Andrew Friedman,
• Margarita Ivanova,
• Ravi Pathak,
• Ekaterina Wright

Affiliations

Ozlem Goker-Alpan

Lysosomal & Rare Disorders Research and Treatment Center, Fairfax, VA

Andrew Friedman

Lysosomal & Rare Disorders Research and Treatment Center, Fairfax, VA

Margarita Ivanova

Lysosomal & Rare Disorders Research and Treatment Center, Fairfax, VA

Ravi Pathak

Takeda Pharmaceuticals USA Inc., Lexington, MA

Ekaterina Wright

Takeda Pharmaceuticals USA Inc., Lexington, MA