Sickle cell disease today: a 75-year journey from “first molecular disease” to “first gene-editing therapy”
Marc Shapira,
Mark J. Koury,
Irene Roberts
Affiliations
Marc Shapira
Faculty of Biology and Medicine, University of Lausanne, Lausanne, Switzerland
Mark J. Koury
Division of Hematology/Oncology, Department of Medicine, Vanderbilt University Medical Center, Nashville, Tennessee, United States
Irene Roberts
Department of Paediatrics and Medical Research Council Molecular Haematology Unit, Weatherhall Institute of Molecular Medicine, Oxford University, Oxford, United Kingdom