JACC: Advances (Aug 2025)
Sex Differences in Children and Adolescents With Hypertrophic Cardiomyopathy
- Gabrielle Norrish, PhD,
- Kimberley Hall, BSc,
- Ella Field, MSc,
- Elena Cervi, MD,
- Olga Boleti, MD,
- Lidia Ziółkowska, MD,
- Iacopo Olivotto, MD,
- Sylvia Passantino, MD,
- Diala Khraiche, MD,
- Giuseppe Limongelli, MD,
- Robert G. Weintraub, MD,
- Aris Anastasakis, MD,
- Elena Biagini, MD,
- Luca Ragni, MD,
- Georgia Sarquella-Brugada, MD,
- Sergi Cesar, MD,
- Terrence Prendiville, MD,
- Karen McLeod, MD,
- Maria Ilina, MD,
- Anwar Baban, MD,
- Tiina H. Ojala, MD,
- Georgia Spentzou, MD,
- Vinay Bhole, MD,
- Feran Gran, MD,
- Elspeth Brown, MD,
- Grazia Delle Donne, MD,
- Bernadette Khodaghalian, MD,
- Adrian Fernandez, MD,
- Piers E.F. Daubeney, MD,
- Katie Linter, MD,
- Peter Kubus, MD,
- Orhan Uzun, MD,
- Regina Bökenkamp, MD,
- Francesca Raimondi, MD,
- Chiara Marrone, MD,
- Constantio Medrano, MD,
- Esther Gonzalez-Lopez, MD,
- Ana Siles, MD,
- Katarzyna Luczak-Wozniak, MD,
- Tara Bharucha, MD,
- Satish Adwani, MD,
- Sabine Klaassen, MD,
- Fernando J. Castro, MD,
- Luis Guereta, MD,
- Hirokuni Yamazawa, MD,
- Gianfranco Sinagra, MD,
- Anca Popoiu, MD,
- Francesca Perin, MD,
- B. Chana, MD,
- Hans De Wilde, MD,
- Torsten.B. Rasmussen, MD,
- Jens Mogensen, MD,
- Sujeev Mathur, MD,
- Fernando Centeno, MD,
- Zdenka Reinhardt, MD,
- Roberto Barriales-Villa, MD,
- Toru Kubo, MD,
- Tiziana Felice, MD,
- Cristina Radulescu, MD,
- Sylvie Schouvey, MD,
- Melissa Chaker, MD,
- Juan Pablo Kaski, MD
Affiliations
- Gabrielle Norrish, PhD
- Centre for Inherited Cardiovascular Diseases, Great Ormond Street Hospital, London, United Kingdom; Department of Cardiology, Institute of Cardiovascular Sciences University College London, London, United Kingdom
- Kimberley Hall, BSc
- Centre for Inherited Cardiovascular Diseases, Great Ormond Street Hospital, London, United Kingdom; Department of Cardiology, University of Exeter, Exeter, United Kingdom
- Ella Field, MSc
- Centre for Inherited Cardiovascular Diseases, Great Ormond Street Hospital, London, United Kingdom
- Elena Cervi, MD
- Centre for Inherited Cardiovascular Diseases, Great Ormond Street Hospital, London, United Kingdom
- Olga Boleti, MD
- Department of Cardiology, Institute of Cardiovascular Sciences University College London, London, United Kingdom
- Lidia Ziółkowska, MD
- Department of Cardiology, The Children’s Memorial Health Institute, Warsaw, Poland
- Iacopo Olivotto, MD
- Department of Cardiology, Meyer Children’s Hospital IRCSS, Florence, Italy
- Sylvia Passantino, MD
- Department of Cardiology, Meyer Children’s Hospital IRCSS, Florence, Italy
- Diala Khraiche, MD
- Department of Cardiology, Necker –Enfants Malades Hospital, Paris, France
- Giuseppe Limongelli, MD
- Department of Cardiology, Monaldi Hospital, Naples, Italy
- Robert G. Weintraub, MD
- Department of Cardiology, The Royal Children’s Hospital, Melbourne, Australia; Department of Cardiology, University of Melbourne, Melbourne, Australia; Department of Cardiology, Murdoch Children’s Research Institute, Parkville, Australia
- Aris Anastasakis, MD
- Department of Cardiology, Onassis Cardiac Surgery Center, Athens, Greece
- Elena Biagini, MD
- Cardiology Unit, Cardiac Thoracic and Vascular Department, IRCCS Azienda Ospedaliero-Universitaria di Bologna, Bologna, Italy; European Reference Network for Rare, Low Prevalence and Complex Diseases of the Heart-ERN GUARD-Heart, Amsterdam, the Netherlands
- Luca Ragni, MD
- Cardiology Unit, Cardiac Thoracic and Vascular Department, IRCCS Azienda Ospedaliero-Universitaria di Bologna, Bologna, Italy
- Georgia Sarquella-Brugada, MD
- European Reference Network for Rare, Low Prevalence and Complex Diseases of the Heart-ERN GUARD-Heart, Amsterdam, the Netherlands; Arrhythmia, Inherited Cardiac Diseases and Sudden Death Unit, Hospital Sant Joan de Déu, Esplugues de Llobregat, Barcelona, Spain; Arrítmies Pediàtriques, Cardiologia Genètica i Mort Sobtada, Malalties Cardiovasculars en el Desenvolupament, Institut de Recerca Sant Joan de Déu (IRSJD), Esplugues de Llobregat, Barcelona, Spain; Medical Science Department, School of Medicine, Universitat de Girona, Girona, Spain; Pediatrics Department, School of Medicine, Universitat de Barcelona, Barcelona, Spain
- Sergi Cesar, MD
- Arrhythmia, Inherited Cardiac Diseases and Sudden Death Unit, Hospital Sant Joan de Déu, Esplugues de Llobregat, Barcelona, Spain; Arrítmies Pediàtriques, Cardiologia Genètica i Mort Sobtada, Malalties Cardiovasculars en el Desenvolupament, Institut de Recerca Sant Joan de Déu (IRSJD), Esplugues de Llobregat, Barcelona, Spain; Medical Science Department, School of Medicine, Universitat de Girona, Girona, Spain
- Terrence Prendiville, MD
- Department of Cardiology, Our Lady’s Children’s Hospital, Dublin, Ireland
- Karen McLeod, MD
- Department of Cardiology, Royal Hospital for Children, Glasgow, United Kingdom
- Maria Ilina, MD
- Department of Cardiology, Royal Hospital for Children, Glasgow, United Kingdom
- Anwar Baban, MD
- Department of Cardiology, Bambino Gesu Hospital, Rome, Italy; Department Clinical Molecular Genetics and Precision Medicine, Mediclinic City Hospital, Dubai, UAE
- Tiina H. Ojala, MD
- Department of Pediatric Cardiology, New Children’s Hospital, University of Helsinki, Helsinki, Finland
- Georgia Spentzou, MD
- Department of Cardiology, Bristol Royal Hospital for Children, Bristol, United Kingdom
- Vinay Bhole, MD
- Department of Cardiology, Birmingham Children’s Hospital, Birmingham, United Kingdom
- Feran Gran, MD
- Department of Cardiology, Val D’Hebron University Hospital, Barcelona, Spain
- Elspeth Brown, MD
- Department of Cardiology, Val D’Hebron University Hospital, Barcelona, Spain
- Grazia Delle Donne, MD
- Department of Cardiology, Leeds General Infirmary, Leeds, United Kingdom
- Bernadette Khodaghalian, MD
- Department of Cardiology, Alder Hey Children’s Hospital, Liverpool, United Kingdom
- Adrian Fernandez, MD
- Department of Cardiology, Fundación Favaloro University Hospital, Buenos Aires, Argentina
- Piers E.F. Daubeney, MD
- Department of Cardiology, Royal Brompton and Harefield NHS Trust, London, United Kingdom
- Katie Linter, MD
- Department of Cardiology, Glenfield Hospital, Leicester, United Kingdom
- Peter Kubus, MD
- Department of Cardiology, University Hospital Motol, Prague, Czech Republic
- Orhan Uzun, MD
- Department of Cardiology, University Hospital of Wales, Cardiff, United Kingdom
- Regina Bökenkamp, MD
- Department of Cardiology, Leiden University Medical Center, Leiden, the Netherlands
- Francesca Raimondi, MD
- Department of Cardiology, Fondazione Toscana G Monasterio, Massa-Pisa, Pisa, Italy
- Chiara Marrone, MD
- Department of Cardiology, Papa Giovanni XXIII Hospital, Bergamo, Italy
- Constantio Medrano, MD
- Department of Cardiology, Hospital General Universitario Gregorio Marañón, Madrid, Spain; Heart Failure and Inherited Cardiac Diseases Unit, Department of Cardiology, Hospital Universitario Puerta de Hierro Majadahonda, IDIPHISA, CIBERCV, Madrid, Spain
- Esther Gonzalez-Lopez, MD
- Heart Failure and Inherited Cardiac Diseases Unit, Department of Cardiology, Hospital Universitario Puerta de Hierro Majadahonda, IDIPHISA, CIBERCV, Madrid, Spain
- Ana Siles, MD
- Department of Pediatrics, Hospital Universitario Puerta de Hierro Majadahonda, Madrid, Spain
- Katarzyna Luczak-Wozniak, MD
- Department of Pediatric Cardiology and General Pediatrics, Medical University of Warsaw, Warsaw, Poland
- Tara Bharucha, MD
- Department of Cardiology, Southampton General Hospital, Southampton, United Kingdom
- Satish Adwani, MD
- Department of Cardiology, John Radcliffe Hospital, Oxford, United Kingdom; Department of Pediatric Cardiology, Deutsches Herzzentrum der Charité, Berlin, Germany; Experimental and Clinical Research Center (ECRC), a Joint Cooperation Between the Charité Medical Faculty and the Max-Delbrück-Center for Molecular Medicine (MDC), Charite – Universitatsmedizin Berlin, Berlin, Germany
- Sabine Klaassen, MD
- DZHK (German Centre for Cardiovascular Research), Partner Site Berlin, Berlin, Germany
- Fernando J. Castro, MD
- Department of Cardiology, University Hospital Virgen de la Arrixaca, Murcia, Spain
- Luis Guereta, MD
- Department of Cardiology, University Hospital La Paz, Madrid, Spain
- Hirokuni Yamazawa, MD
- Department of Pediatrics, Faculty of Medicine and Graduate School of Medicine, Hokkaido University Hospital, Sapporo, Japan
- Gianfranco Sinagra, MD
- Heart Muscle Disease Registry Trieste, University of Trieste, Trieste, Italy
- Anca Popoiu, MD
- University of Medicine and Pharmacy ''Victor Babes'' Timisoara, Department of Pediatrics, Children’s Hospital ‘Louis Turcanu’, Timisoara, Romania
- Francesca Perin, MD
- Department of Cardiology, Hospital Universitario Virgen de las Nieves, Granada, Spain
- B. Chana, MD
- Department of Cardiology, Ospedaliero Universitaria di Parma, Parma, Italy
- Hans De Wilde, MD
- Department of Cardiology, Ghent University Hospital, Ghent, Belgium
- Torsten.B. Rasmussen, MD
- Department of Cardiology, Aarhus University Hospital, Aarhus, Denmark
- Jens Mogensen, MD
- Department of Cardiology, Odense University Hospital, Odense, Denmark
- Sujeev Mathur, MD
- Department of Cardiology, Evelina Children’s Hospital, London, United Kingdom
- Fernando Centeno, MD
- Department of Cardiology, Rio Hortega University Hospital, Valladolid, Spain
- Zdenka Reinhardt, MD
- Department of Cardiology, The Freeman Hospital, Newcastle, United Kingdom
- Roberto Barriales-Villa, MD
- Complexo Hospitalario Universitario A Coruna, INIBIC, CIBERCV, Coruna, Spain
- Toru Kubo, MD
- Department of Cardiology, Kochi Medical School Hospital, Kochi, Japan
- Tiziana Felice, MD
- Department of Cardiology, Mater Dei Hospital, Msida, Malta
- Cristina Radulescu, MD
- Department of Cardiology, UMPCD Bucharest, Bucharest, Romania
- Sylvie Schouvey, MD
- Department of Cardiology, Hospital Saint Joseph, Marseille, France
- Melissa Chaker, MD
- Department of Cardiology, Hospital Garrahan, Buenos Aires, Argentina
- Juan Pablo Kaski, MD
- Centre for Inherited Cardiovascular Diseases, Great Ormond Street Hospital, London, United Kingdom; Department of Cardiology, Institute of Cardiovascular Sciences University College London, London, United Kingdom; Address for correspondence: Dr Juan Pablo Kaski, Centre for Paediatric Inherited and Rare Cardiovascular Disease, UCL Institute of Cardiovascular Science, London WC1N 1DZ, United Kingdom.
- DOI
- https://doi.org/10.1016/j.jacadv.2025.101907
- Journal volume & issue
-
Vol. 4,
no. 8
p. 101907
Abstract
Background: Sex differences have been described in adults with hypertrophic cardiomyopathy (HCM), but it is unknown if similar differences exist in childhood-onset disease. Objectives: This study aimed to investigate the influence of biological sex on the clinical characteristics and outcomes of children with HCM. Methods: An international retrospective cohort of patients diagnosed with nonsyndromic HCM ≤16 years was formed. Sex differences in baseline characteristics and clinical outcomes were investigated. Primary outcome was all-cause mortality or cardiac transplantation. Secondary outcomes include major arrhythmic cardiac event and heart failure event. Results: Of 1,433 patients diagnosed at a median age of 11 years (IQR: 6-14), 471 (33.0%) were female. Although there were no sex differences in phenotype in preadolescent patients (<12 years), adolescent female patients were more likely to have heart failure symptoms (n = 53 [31.9%] vs n = 86 [22.5%]; P = 0.019). Adolescent female patients had larger left atrial size (1.4 z-score [±2.3] vs 2.1 z-score [±2.5]; P = 0.0056) but there was no difference in degree of hypertrophy or proportion with obstructive disease. Over a median follow-up of 5.3 years (IQR: 2.9, 8.0) annual incidence of all-cause mortality or cardiac transplantation, major arrhythmic cardiac event or heart failure events did not vary by sex. Conclusions: Young female patients with HCM are more likely to experience heart failure symptoms and have echocardiographic features of diastolic impairment. Despite differences in phenotype, outcomes during childhood and young adulthood are not different. Further studies are required to explore the underlying mechanisms for these observed differences.
Keywords