Access to novel therapies for Duchenne muscular dystrophy—Insights from expert treating physicians

• Aravindhan Veerapandiyan,
• Anne M. Connolly,
• Katherine D. Mathews,
• Stanley Nelson,
• Craig McDonald,
• Richard S. Finkel,
• Vettaikorumakankav Vedanarayanan,
• Cuixia Tian,
• Susan Apkon,
• Julie A. Parsons,
• Jonathan H. Soslow,
• William Bryan Burnette,
• Kaitlin Y. Batley,
• Susan T. Iannaccone,
• Carolina Tesi Rocha,
• Kevin M. Flanigan,
• Diana Bharucha‐Goebel,
• Sarah Wright,
• Migvis Monduy,
• Simona Treidler,
• Ashutosh Kumar,
• Nancy L. Kuntz,
• Vamshi K. Rao,
• Rachel Schrader,
• Saunder M. Bernes,
• Vikki Ann Stefans,
• Jena M. Krueger,
• Marcia V. Felker,
• Omer Abdul Hamid,
• Arpita Lakhotia,
• Susan Matesanz,
• Partha S. Ghosh,
• Natalie Katz,
• Hoda Abdel‐Hamid,
• Chamindra G. Laverty,
• Bo Hoon Lee,
• Amy Harper,
• Leigh Ramos‐Platt,
• Diana Castro,
• Russell J. Butterfield,
• Crystal M. Proud,
• Craig M. Zaidman,
• Emma Ciafaloni

Affiliations

Aravindhan Veerapandiyan

University of Arkansas for Medical Sciences, Arkansas Children's Hospital Little Rock Arkansas USA

Anne M. Connolly

Nationwide Children's Hospital The Ohio State University Columbus Ohio USA

Katherine D. Mathews

University of Iowa Carver College of Medicine Iowa City Iowa USA

Stanley Nelson

David Geffen School of Medicine at University of California Los Angeles Los Angeles California USA

Craig McDonald

University of California Davis Health Sacramento California USA

Richard S. Finkel

St. Jude Children's Research Hospital Memphis Tennessee USA

Vettaikorumakankav Vedanarayanan

The University of Texas at Austin Dell Medical School Austin Texas USA

Cuixia Tian

Cincinnati Children's Hospital Medical Center & College of Medicine University of Cincinnati Cincinnati Ohio USA

Susan Apkon

University of Colorado School of Medicine, Children's Hospital Colorado Aurora Colorado USA

Julie A. Parsons

University of Colorado School of Medicine, Children's Hospital Colorado Aurora Colorado USA

Jonathan H. Soslow

Vanderbilt University Medical Center Nashville Tennessee USA

William Bryan Burnette

Vanderbilt University Medical Center Nashville Tennessee USA

Kaitlin Y. Batley

UT Southwestern Medical Center Dallas Texas USA

Susan T. Iannaccone

UT Southwestern Medical Center Dallas Texas USA

Carolina Tesi Rocha

Stanford University Palo Alto California USA

Kevin M. Flanigan

Nationwide Children's Hospital The Ohio State University Columbus Ohio USA

Diana Bharucha‐Goebel

Children's National Medical Center Washington District of Columbia USA

Sarah Wright

Children's National Medical Center Washington District of Columbia USA

Migvis Monduy

Niklaus Children's Hospital Miami Florida USA

Simona Treidler

Stony Brook University Stony Brook New York USA

Ashutosh Kumar

Penn State Health Milton S. Hershey Medical Center Hershey Pennsylvania USA

Nancy L. Kuntz

Ann & Robert H. Lurie Children's Hospital of Chicago Northwestern University Feinberg School of Medicine Chicago Illinois USA

Vamshi K. Rao

Ann & Robert H. Lurie Children's Hospital of Chicago Northwestern University Feinberg School of Medicine Chicago Illinois USA

Rachel Schrader

Parent Project Muscular Dystrophy Washington District of Columbia USA

Saunder M. Bernes

University of Arizona College of Medicine, Barrow Neurological Institute at Phoenix Children's Phoenix Arizona USA

Vikki Ann Stefans

University of Arkansas for Medical Sciences, Arkansas Children's Hospital Little Rock Arkansas USA

Jena M. Krueger

Helen DeVos Children's Hospital, Corewell Health Grand Rapids Michigan USA

Marcia V. Felker

Indiana University School of Medicine, Riley Children's Indianapolis Indiana USA

Omer Abdul Hamid

Nemours Children's Health Orlando Florida USA

Arpita Lakhotia

University of Louisville, Norton Children's Medical Group Louisville Kentucky USA

Susan Matesanz

Children's Hospital of Philadelphia Philadelphia Pennsylvania USA

Partha S. Ghosh

Boston Children's Hospital Boston Massachusetts USA

Natalie Katz

Duke University Medical Center Durham North Carolina USA

Hoda Abdel‐Hamid

UPMC Children's Hospital of Pittsburgh University of Pittsburgh Pittsburgh Pennsylvania USA

Chamindra G. Laverty

University of California San Diego San Diego California USA

Bo Hoon Lee

University of Rochester Medical Center Rochester New York USA

Amy Harper

Children's Hospital of Richmond Richmond Virginia USA

Leigh Ramos‐Platt

Keck School of Medicine University of Southern California and Children's Hospital of Los Angeles Los Angeles California USA

Diana Castro

Neurology and Neuromuscular Care Center Denton Texas USA

Russell J. Butterfield

University of Utah Salt Lake City Utah USA

Crystal M. Proud

Children's Hospital of The King's Daughters Norfolk Virginia USA

Craig M. Zaidman

Washington University School of Medicine and St. Louis Children's Hospital St. Louis Missouri USA

Emma Ciafaloni

University of Rochester Medical Center Rochester New York USA