PB2508: COMPARING DEFINITIONS OF EPISODES OF VASO-OCCLUSION AS ENDPOINTS IN CLINICAL STUDIES OF SICKLE CELL DISEASE

• Franco Locatelli,
• Nanxin LI,
• Suzan Imren,
• Fengjuan Xuan,
• Jaime Rubin,
• Bill Hobbs,
• Haydar Frangoul

Affiliations

Franco Locatelli

1 IRCCS, Ospedale Pediatrico Bambino Gesù Rome, Catholic University of the Sacred Heart, Rome, Italy

Nanxin LI

2 Vertex Pharmaceuticals Incorporated, Boston, MA, United States

Suzan Imren

2 Vertex Pharmaceuticals Incorporated, Boston, MA, United States

Fengjuan Xuan

2 Vertex Pharmaceuticals Incorporated, Boston, MA, United States

Jaime Rubin

2 Vertex Pharmaceuticals Incorporated, Boston, MA, United States

Bill Hobbs

2 Vertex Pharmaceuticals Incorporated, Boston, MA, United States

Haydar Frangoul

3 Sarah Cannon Center for Blood Cancer at The Children’s Hospital at TriStar Centennial, Nashville, TN, United States