PLoS ONE (Jan 2024)
Meaningful changes in motor function in Duchenne muscular dystrophy (DMD): A multi-center study
- Francesco Muntoni,
- James Signorovitch,
- Gautam Sajeev,
- Nicolae Done,
- Zhiwen Yao,
- Nathalie Goemans,
- Craig McDonald,
- Eugenio Mercuri,
- Erik H. Niks,
- Brenda Wong,
- Krista Vandenborne,
- Volker Straub,
- Imelda J. M. de Groot,
- Cuixia Tian,
- Adnan Manzur,
- Ibrahima Dieye,
- Henry Lane,
- Susan J. Ward,
- Laurent Servais
Affiliations
- Francesco Muntoni
- James Signorovitch
- Gautam Sajeev
- Nicolae Done
- Zhiwen Yao
- Nathalie Goemans
- Craig McDonald
- Eugenio Mercuri
- Erik H. Niks
- Brenda Wong
- Krista Vandenborne
- Volker Straub
- Imelda J. M. de Groot
- Cuixia Tian
- Adnan Manzur
- Ibrahima Dieye
- Henry Lane
- Susan J. Ward
- Laurent Servais
- Journal volume & issue
-
Vol. 19,
no. 7