PLoS ONE (Jan 2024)

Meaningful changes in motor function in Duchenne muscular dystrophy (DMD): A multi-center study

  • Francesco Muntoni,
  • James Signorovitch,
  • Gautam Sajeev,
  • Nicolae Done,
  • Zhiwen Yao,
  • Nathalie Goemans,
  • Craig McDonald,
  • Eugenio Mercuri,
  • Erik H. Niks,
  • Brenda Wong,
  • Krista Vandenborne,
  • Volker Straub,
  • Imelda J. M. de Groot,
  • Cuixia Tian,
  • Adnan Manzur,
  • Ibrahima Dieye,
  • Henry Lane,
  • Susan J. Ward,
  • Laurent Servais

Journal volume & issue
Vol. 19, no. 7

Abstract

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