P1520: AN ACTIVIN RECEPTOR IIB LIGAND TRAP, IN COMBINATION WITH TMPRSS6 INDUCED IRON-RESTRICTION, IS A SUPERIOR TREATMENT FOR CORRECTING Β-THALASSEMIA IN MICE
A. Guerra,
P. Demsko,
S. Sinha,
P. McVeigh,
C. Castruccio Castracani,
L. Breda,
C. Casu,
S. Guo,
S. Rivella
Affiliations
A. Guerra
1 Pediatrics, Children’s Hospital of Philadelphia
P. Demsko
2 Pediatrics, University of Pennsylvania, Perelman School of Medicine, Philadelphia
S. Sinha
1 Pediatrics, Children’s Hospital of Philadelphia
P. McVeigh
1 Pediatrics, Children’s Hospital of Philadelphia
C. Castruccio Castracani
1 Pediatrics, Children’s Hospital of Philadelphia
L. Breda
1 Pediatrics, Children’s Hospital of Philadelphia
C. Casu
1 Pediatrics, Children’s Hospital of Philadelphia
S. Guo
3 Pediatrics, Ionis Pharmaceuticals, Inc., Carlsbad, United States of America