Genetics in Medicine Open (Jan 2024)
P144: Persistence of growth-promoting effects in children with achondroplasia up to 7 years: Update from phase 2 extension study with vosoritide*
- Julie Hoover-Fong,
- Melita Irving,
- Carlos Bacino,
- Joel Charrow,
- Carlos Prada,
- Valerie Cormier-Daire,
- Lynda Polgreen,
- Paul Harmatz,
- Sajda Ghani,
- Elena Fisheleva,
- Andrea Low,
- Jonathan Day,
- John Phillips, III,
- Ravi Savarirayan
Affiliations
- Julie Hoover-Fong
- Johns Hopkins, Department of Pediatrics, Baltimore, MD
- Melita Irving
- Guy’s and St. Thomas’ NHS Foundation Trust, Evelina Children’s Hospital, London, UK
- Carlos Bacino
- Baylor College of Medicine, Houston, TX
- Joel Charrow
- Ann and Robert H. Lurie Children’s Hospital of Chicago, Chicago, IL
- Carlos Prada
- Ann and Robert H. Lurie Children’s Hospital of Chicago, Chicago, IL
- Valerie Cormier-Daire
- Paris University, Hopital Necker – Enfants Malades, Paris, France
- Lynda Polgreen
- Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center, David Geffen School of Medicine – UCLA, CA
- Paul Harmatz
- UCSF Benioff Children’s Hospital Oakland, Oakland, CA
- Sajda Ghani
- BioMarin (U.K.) Limited, London, UK
- Elena Fisheleva
- BioMarin (U.K.) Limited, London, UK
- Andrea Low
- BioMarin Pharmaceutical, Novato, CA
- Jonathan Day
- BioMarin (U.K.) Limited, London, UK
- John Phillips, III
- Vanderbilt University Medical Center, Nashville, TN
- Ravi Savarirayan
- Murdoch Children’s Research Institute, Royal Children’s Hospital, and University of Melbourne, Parkville, Australia
- Journal volume & issue
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Vol. 2
p. 101041