Genetics in Medicine Open (Jan 2023)
P194: Persistence of growth promoting effects in children with achondroplasia over seven years: Update from phase II extension study with vosoritide*
- Julie Hoover-Fong,
- Melita Irving,
- Carlos Bacino,
- Joel Charrow,
- Valérie Cormier-Daire,
- Lynda Polgreen,
- Paul Harmatz,
- Alice Huntsman-Labed,
- Elena Fisheleva,
- Ian Sabir,
- Jonathan Day,
- John Phillips,
- Ravi Savarirayan
Affiliations
- Julie Hoover-Fong
- McKusick-Nathans Department of Genetic Medicine, Johns Hopkins University, Baltimore, MD
- Melita Irving
- Guy’s and St. Thomas’ NHS Foundation Trust, Evelina Children's Hospital, London, UK
- Carlos Bacino
- Baylor College of Medicine, Houston, TX
- Joel Charrow
- Ann and Robert H. Lurie Children’s Hospital of Chicago, Chicago, IL
- Valérie Cormier-Daire
- Centre of Reference for Constitutional Bone Diseases (MOC), Department of Clinical Genetics, Paris Centre University, INSERM, Imagine Institute, Necker-Enfants Malades Hospital, Paris, France
- Lynda Polgreen
- Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center, Torrance, CA
- Paul Harmatz
- UCSF Benioff Children’s Hospital Oakland, Oakland, CA
- Alice Huntsman-Labed
- BioMarin (UK) Limited, London, UK
- Elena Fisheleva
- BioMarin (UK) Limited, London, UK
- Ian Sabir
- BioMarin (UK) Limited, London, UK
- Jonathan Day
- BioMarin (UK) Limited, London, UK
- John Phillips
- Vanderbilt University Medical Center, Nashville, TN
- Ravi Savarirayan
- Murdoch Children’s Research Institute, Royal Children’s Hospital, and University of Melbourne, Parkville, Victoria, Australia
- Journal volume & issue
-
Vol. 1,
no. 1
p. 100223