Toward a translational gene therapy for mucolipidosis IV

• Brina Snyder,
• Rachel M. Bailey

Affiliations

Brina Snyder

Center for Alzheimer’s and Neurodegenerative Diseases, University of Texas Southwestern Medical School, 5323 Harry Hines Blvd., Dallas, TX 75235, USA

Rachel M. Bailey

Center for Alzheimer’s and Neurodegenerative Diseases, University of Texas Southwestern Medical School, 5323 Harry Hines Blvd., Dallas, TX 75235, USA; Department of Pediatrics, University of Texas Southwestern Medical School, 5323 Harry Hines Blvd., Dallas, TX 75235, USA; Corresponding author: Rachel M. Bailey, Department of Pediatrics, University of Texas Southwestern Medical School, 5323 Harry Hines Blvd., Dallas, TX 75235, USA.