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Frontiers in Genome Editing
(Mar 2023)
Editorial: Genome and transcriptome editing to understand and treat neuromuscular diseases
Rika Maruyama,
Alyson Fiorillo,
Christopher Heier,
Dongsheng Duan,
Toshifumi Yokota
Affiliations
Rika Maruyama
Department of Medical Genetics, University of Alberta Faculty of Medicine and Dentistry, Edmonton, AB, Canada
Alyson Fiorillo
Center for Genetic Medicine Research, Children’s National Hospital, Washington, DC, United States
Christopher Heier
Center for Genetic Medicine Research, Children’s National Hospital, Washington, DC, United States
Dongsheng Duan
Department of Molecular Microbiology and Immunology, School of Medicine, The University of Missouri, Columbia, MO, United States
Toshifumi Yokota
Department of Medical Genetics, University of Alberta Faculty of Medicine and Dentistry, Edmonton, AB, Canada
DOI
https://doi.org/10.3389/fgeed.2023.1176699
Journal volume & issue
Vol. 5
Abstract
Read online
No abstracts available.
Keywords
amyotrophic lateral sclerosis
5′UTR
shRNAs
antisense oligonucleotides
GNE
microRNA
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