3024 COMET post hoc analysis: efficacy of long-term avalglucosidase alfa in subgroups of patients with late-onset Pompe disease

• Mark Roberts,
• Jordi Diaz-Manera,
• Antonio Toscano,
• Sabrina Sacconi,
• Mazen M Dimachkie,
• Nicole Armstrong,
• Robert Henderson,
• Benedikt Schoser,
• Priya S Kishnani,
• Olivier Huynh-Ba,
• Nathan Thibault,
• Young Chul Choi,
• Shugo Suwazono,
• Paulo Victor Sgobbi de Souza,
• Magali Periquet

Affiliations

Mark Roberts

14Salford Royal NHS Foundation Trust, Salford, West Sussex, UK

Jordi Diaz-Manera

7John Walton Muscular Dystrophy Research Centre, Newcastle University and Newcastle Hospitals NHS Foundation Trust, Newcastle Upon Tyne, UK

Antonio Toscano

8Department of Clinical and Experimental Medicine, Reference Center for Rare Neuromuscular Disorders, University of Messina, Messina, Italy

Sabrina Sacconi

8 Peripheral Nervous System, Muscle and ALS Department, Université Côte d’Azur, Nice, France

Mazen M Dimachkie

Department of Neurology, University of Kansas City Medical Center, Kansas City, Missouri, USA

Nicole Armstrong

11Sanofi, Cambridge, MA, USA

Robert Henderson

1Department of Neurology, Royal Brisbane and Women’s Hospital and Wesley Hospital, Brisbane, QL:D, Australia

Benedikt Schoser

2Department of Neurology, Friedrich-Baur-Institute, LMU Klinikum München, München, Germany

Priya S Kishnani

3Division of Medical Genetics, Department of Pediatrics, Duke University Medical Center, Durham, NC, USA

Olivier Huynh-Ba

19Sanofi, Chilly-Mazarin, France

Nathan Thibault

20Sanofi, Cambridge, MA, USA

Young Chul Choi

17Gangnam Severance Hospital, Yonsei University, College of Medicine, Seoul, Korea

Shugo Suwazono

7Division of Neurology, National Hospital Organization Okinawa Hospital, Okinawa, Japan

Paulo Victor Sgobbi de Souza

9Paulista School of Medicine, Federal University of São Paulo, São Paulo, Brazil

Magali Periquet

13Sanofi, Berlin, Germany