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Genetics in Medicine Open
(Jan 2023)
O08: Long-term efficacy and safety of pegzilarginase for arginase 1 deficiency: 2 years of experience in the phase 2 extension study*
Markey McNutt,
George Diaz,
Andreas Schulze,
Gillian Bubb,
Leslie Sloan,
Elisa Leão-Teles,
Spyros Batzios,
Angela Sun,
Allison Bannick,
Roberto Zori,
Gregory Enns
Affiliations
Markey McNutt
UT Southwestern Medical Center
George Diaz
Icahn School of Medicine at Mount Sinai
Andreas Schulze
University of Toronto and The Hospital for Sick Children
Gillian Bubb
Aeglea BioTherapeutics, Inc.
Leslie Sloan
Aeglea BioTherapeutics, Inc.
Elisa Leão-Teles
Centro Hospitalar de São João
Spyros Batzios
Great Ormond Street Hospital NHS Trust
Angela Sun
University of Washington and Seattle Children's Hospital
Allison Bannick
Children's Hospital of Michigan, Wayne State University
Roberto Zori
University of Florida
Gregory Enns
Stanford University and Lucile Packard Children’s Hospital
Journal volume & issue
Vol. 1, no. 1
p. 100009
Abstract
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