Journal of Clinical Medicine (Jun 2023)

Reply to Mistry et al. The Two Substrate Reduction Therapies for Type 1 Gaucher Disease Are Not Equivalent. Comment on “Hughes et al. Switching between Enzyme Replacement Therapies and Substrate Reduction Therapies in Patients with Gaucher Disease: Data from the Gaucher Outcome Survey (GOS). <i>J. Clin. Med.</i> 2022, <i>11</i>, 5158”

  • Derralynn A. Hughes,
  • Patrick Deegan,
  • Pilar Giraldo,
  • Özlem Göker-Alpan,
  • Heather Lau,
  • Elena Lukina,
  • Shoshana Revel-Vilk,
  • Maurizio Scarpa,
  • Jaco Botha,
  • Noga Gadir,
  • Ari Zimran

DOI
https://doi.org/10.3390/jcm12124017
Journal volume & issue
Vol. 12, no. 12
p. 4017

Abstract

Read online

Thank you for allowing us the opportunity to respond to the commentary from Mistry and colleagues (Comment: The two substrate reduction therapies for type 1 Gaucher disease are not equivalent) [...]

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