P005: Head-to-head trial of pegunigalsidase alfa vs agalsidase beta in Fabry disease: Phase 3 randomized, double-blind, BALANCE Study 2-year results

• John Bernat,
• Eric Wallace,
• Ozlem Goker-Alpan,
• William Wilcox,
• Myrl Holida,
• Nicola Longo,
• Derralynn Hughes,
• Pilar Giraldo,
• Maria Molnar,
• Damara Ortiz,
• Robert Hopkin,
• Camilla Tondel,
• Ales Linhart,
• Patrick Deegan,
• Ana Jovanovic,
• Michael Muriello,
• Bruce Barshop,
• Virginia Kimonis,
• Bojan Vujkovac,
• Albina Nowak,
• Tarekegn Hiwot,
• Antonio Pisani,
• Dominique Germain,
• Ilkka Kantola,
• Jasmine Knoll,
• Ankit Mehta,
• Stephen Waldek,
• Einat Almon,
• Sari Alon,
• Raul Chertkoff,
• Rossana Rocco,
• David Warnock

Affiliations

John Bernat

University of Iowa Hospitals and Clinics, Iowa City, IA

Eric Wallace

The University of Alabama at Birmingham, Birmingham, AL

Ozlem Goker-Alpan

Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax, VA

William Wilcox

Department of Human Genetics, Emory University, Atlanta, GA

Myrl Holida

University of Iowa Hospitals and Clinics, Iowa City, IA

Nicola Longo

University of Utah, Center for Clinical Translational Sciences, Salt Lake City, UT

Derralynn Hughes

Lysosomal Storage Disorders Unit, Royal Free London NHS Foundation Trust and University College London, London, UK

Pilar Giraldo

Quironsalud Hospital, Zaragoza, Spain

Maria Molnar

Institute of Genomic Medicine and Rare Disorders, Semmelweis University, Budapest, HUN

Damara Ortiz

UPMC Children’s Hospital of Pittsburgh, Pittsburgh, PA

Robert Hopkin

Cincinnati Children’s Hospital Medical Center, Cincinnati, OH

Camilla Tondel

Haukeland University Hospital, Renal Research Group, Bergen, NOR

Ales Linhart

Vseobecna fakultni nemocnice v Praze, Praha, CZE

Patrick Deegan

Addenbrooke’s Hospital, Cambridge University Hospitals, Cambridge, UK

Ana Jovanovic

Mark Holland Metabolic Unit, Northern Care Alliance NHS Foundation Trust, Greater Manchester, UK

Michael Muriello

Department of Pediatrics – Genetics Curative Network Building, Milwaukee, WI

Bruce Barshop

University of California San Diego, La Jolla, CA

Virginia Kimonis

University of California, Irvine institute for Clinical and Translational Science, CA

Bojan Vujkovac

Slovenj Gradec General Hospital, Slovenj Gradec, SI

Albina Nowak

University Hospital of Psychiatry Zürich, Department of internal medicine, CHE

Tarekegn Hiwot

Queen Elizabeth Hospital Birmingham, Edgbaston, Birmingham West Midlands, UK

Antonio Pisani

Azienda Ospedaliera Universitaria ''Federico II'', Dipartimento di Sanita Pubblica, Napoli, ITA

Dominique Germain

University of Versailles, Division of Medical Genetics, Garches, FRA

Ilkka Kantola

Department of Medicine, Turku University Hospital, Turku, FIN

Jasmine Knoll

Phoenix Children’s Hospital, Phoenix, AZ

Ankit Mehta

Baylor University Medical Center, Dallas, TX

Stephen Waldek

University of Sunderland, Sunderland, UK

Einat Almon

Protalix Biotherapeutics, Carmiel, ISL

Sari Alon

Protalix Biotherapeutics, Carmiel, ISL

Raul Chertkoff

Protalix Biotherapeutics, Carmiel, ISL

Rossana Rocco

Chiesi Farmaceutici S.p.A., Parma, ITA

David Warnock

The University of Alabama at Birmingham, Birmingham, AL