Frontiers in Neurology (Dec 2023)
Predictors of treatment switching in the Big Multiple Sclerosis Data Network
- Tim Spelman,
- Tim Spelman,
- Melinda Magyari,
- Melinda Magyari,
- Helmut Butzkueven,
- Helmut Butzkueven,
- Anneke Van Der Walt,
- Anneke Van Der Walt,
- Sandra Vukusic,
- Sandra Vukusic,
- Sandra Vukusic,
- Maria Trojano,
- Pietro Iaffaldano,
- Dana Horáková,
- Jirí Drahota,
- Fabio Pellegrini,
- Fabio Pellegrini,
- Robert Hyde,
- Pierre Duquette,
- Jeannette Lechner-Scott,
- Jeannette Lechner-Scott,
- Seyed Aidin Sajedi,
- Patrice Lalive,
- Vahid Shaygannejad,
- Serkan Ozakbas,
- Sara Eichau,
- Raed Alroughani,
- Murat Terzi,
- Marc Girard,
- Tomas Kalincik,
- Francois Grand'Maison,
- Olga Skibina,
- Samia J. Khoury,
- Bassem Yamout,
- Maria Jose Sa,
- Oliver Gerlach,
- Yolanda Blanco,
- Rana Karabudak,
- Celia Oreja-Guevara,
- Ayse Altintas,
- Stella Hughes,
- Pamela McCombe,
- Radek Ampapa,
- Koen de Gans,
- Chris McGuigan,
- Aysun Soysal,
- Julie Prevost,
- Nevin John,
- Jihad Inshasi,
- Leszek Stawiarz,
- Ali Manouchehrinia,
- Lars Forsberg,
- Finn Sellebjerg,
- Anna Glaser,
- Luigi Pontieri,
- Hanna Joensen,
- Peter Vestergaard Rasmussen,
- Tobias Sejbaek,
- Mai Bang Poulsen,
- Jeppe Romme Christensen,
- Matthias Kant,
- Morten Stilund,
- Morten Stilund,
- Henrik Mathiesen,
- Jan Hillert,
- The Big MS Data Network: a collaboration of the Czech MS Registry, the Danish MS Registry, Italian MS Registry, Swedish MS Registry, MSBase Study Group, and OFSEP
Affiliations
- Tim Spelman
- Department of Clinical Neuroscience, Karolinska Institute, Stockholm, Sweden
- Tim Spelman
- MSBase Foundation, Melbourne, VIC, Australia
- Melinda Magyari
- The Danish Multiple Sclerosis Registry, Copenhagen University Hospital, Rigshospitalet, Glostrup, Denmark
- Melinda Magyari
- Danish Multiple Sclerosis Center, Department of Neurology, Copenhagen University Hospital Rigshospitalet, Glostrup, Copenhagen, Denmark
- Helmut Butzkueven
- MSBase Foundation, Melbourne, VIC, Australia
- Helmut Butzkueven
- MS and Neuroimmunology Research, Central Clinical School, Alfred and Box Hill Hospitals, Monash University, Melbourne, VIC, Australia
- Anneke Van Der Walt
- MSBase Foundation, Melbourne, VIC, Australia
- Anneke Van Der Walt
- Department of Neuroscience, Central Clinical School, Monash University, Melbourne, VIC, Australia
- Sandra Vukusic
- Service de Neurologie, Sclérose en Plaques, Pathologies de la Myéline et Neuro-Inflammation, Hôpital Neurologique Pierre Wertheimer, Hospices Civils de Lyon, Lyon, France
- Sandra Vukusic
- Centre des Neurosciences de Lyon, L'Institut national de la santé et de la recherche médicale 1028 et Centre national de la recherche scientifique joint research units5292, Lyon, France
- Sandra Vukusic
- Faculté de Médicine Lyon-Est, Université Claude Bernard Lyon 1, Villeurbanne, Auvergne-Rhône-Alpes, France
- Maria Trojano
- 0Department of Basic Medical Sciences, Neurosciences and Sense Organs, University of Bari Aldo Moro, Bari, Italy
- Pietro Iaffaldano
- 1Department of Translational Biomedicine and Neuroscience, DiBraiN, University of Bari Aldo Moro, Bari, Italy
- Dana Horáková
- 2Department of Neurology and Center of Clinical Neuroscience, First Faculty of Medicine, Charles University and General University Hospital, Prague, Czechia
- Jirí Drahota
- 2Department of Neurology and Center of Clinical Neuroscience, First Faculty of Medicine, Charles University and General University Hospital, Prague, Czechia
- Fabio Pellegrini
- 3Biogen International GmbH, Zug, Switzerland
- Fabio Pellegrini
- 4Biogen Digital Health, Biogen Spain, Madrid, Spain
- Robert Hyde
- 3Biogen International GmbH, Zug, Switzerland
- Pierre Duquette
- 5University of Montreal Hospital Research Centre and Universite de Montreal, Montreal, QC, Canada
- Jeannette Lechner-Scott
- 6University Newcastle, Callaghan, NSW, Australia
- Jeannette Lechner-Scott
- 7Hunter Medical Research Institute, Hunter New England Health, John Hunter Hospital, New Lambton Heights, NSW, Australia
- Seyed Aidin Sajedi
- 8Department of Neurology, Neuroscience Research Center, Golestan University of Medical Sciences, Gogan, Iran
- Patrice Lalive
- 9Faculty of Medicine, Division of Neurology, Geneva University Hospital, Geneva, Switzerland
- Vahid Shaygannejad
- 0Isfahan University of Medical Sciences, Isfahan, Iran
- Serkan Ozakbas
- 1Dokuz Eylul University, Konak/Izmir, Türkiye
- Sara Eichau
- 2Department of Neurology, Hospital Universitario Virgen Macarena, Sevilla, Spain
- Raed Alroughani
- 3Division of Neurology, Department of Medicine, Amiri Hospital, Sharq, Kuwait
- Murat Terzi
- 4Medical Faculty, 19 Mayis University, Samsun, Türkiye
- Marc Girard
- 5University of Montreal Hospital Research Centre and Universite de Montreal, Montreal, QC, Canada
- Tomas Kalincik
- 5Clinical Outcomes Research Unit, Department of Medicine, University of Melbourne, Melbourne, VIC, Australia
- Francois Grand'Maison
- 6Neuro Rive-Sud, Longueuil, QC, Canada
- Olga Skibina
- MS and Neuroimmunology Research, Central Clinical School, Alfred and Box Hill Hospitals, Monash University, Melbourne, VIC, Australia
- Samia J. Khoury
- 7Nehme and Therese Tohme Multiple Sclerosis Center, American University of Beirut Medical Center, Beirut, Lebanon
- Bassem Yamout
- 7Nehme and Therese Tohme Multiple Sclerosis Center, American University of Beirut Medical Center, Beirut, Lebanon
- Maria Jose Sa
- 8Department of Neurology, Faculty of Health Sciences, University Fernando Pessoa, Porto, Portugal
- Oliver Gerlach
- 9Academic MS Center Zuyderland, Department of Neurology, Zuyderland Medical Center, Sittard-Geleen, Netherlands
- Yolanda Blanco
- 0Center of Neuroimmunology, Service of Neurology, Hospital Clinic de Barcelona, Barcelona, Spain
- Rana Karabudak
- 1Hacettepe University, Ankara, Türkiye
- Celia Oreja-Guevara
- 2Department of Neurology, Hospital Clinico San Carlos, Madrid, Spain
- Ayse Altintas
- 3Department of Neurology, School of Medicine and Koc University Research Center for Translational Medicine (KUTTAM), Koc University, Istanbul, Türkiye
- Stella Hughes
- 4Royal Victoria Hospital, Belfast, United Kingdom
- Pamela McCombe
- 5University of Queensland, Brisbane, QLD, Australia
- Radek Ampapa
- 6Nemocnice Jihlava, Jihlava, Czechia
- Koen de Gans
- 7Groene Hart Ziekenhuis, Gouda, Netherlands
- Chris McGuigan
- 8St Vincent's University Hospital, Dublin, Ireland
- Aysun Soysal
- 9Bakirkoy Education and Research Hospital for Psychiatric and Neurological Diseases, Istanbul, Türkiye
- Julie Prevost
- 0CSSS Saint-Jérôme, Saint-Jerome, QC, Canada
- Nevin John
- 1Monash Health, Melbourne, VIC, Australia
- Jihad Inshasi
- 2Rashid Hospital, Dubai, United Arab Emirates
- Leszek Stawiarz
- Department of Clinical Neuroscience, Karolinska Institute, Stockholm, Sweden
- Ali Manouchehrinia
- Department of Clinical Neuroscience, Karolinska Institute, Stockholm, Sweden
- Lars Forsberg
- Department of Clinical Neuroscience, Karolinska Institute, Stockholm, Sweden
- Finn Sellebjerg
- Danish Multiple Sclerosis Center, Department of Neurology, Copenhagen University Hospital Rigshospitalet, Glostrup, Copenhagen, Denmark
- Anna Glaser
- Department of Clinical Neuroscience, Karolinska Institute, Stockholm, Sweden
- Luigi Pontieri
- The Danish Multiple Sclerosis Registry, Copenhagen University Hospital, Rigshospitalet, Glostrup, Denmark
- Hanna Joensen
- The Danish Multiple Sclerosis Registry, Copenhagen University Hospital, Rigshospitalet, Glostrup, Denmark
- Peter Vestergaard Rasmussen
- 3Department of Neurology, Aarhus University Hospital, Aarhus, Denmark
- Tobias Sejbaek
- 4Department of Neurology, Southwest Jutland Hospital, University Hospital of Southern Denmark, Esbjerg, Denmark
- Mai Bang Poulsen
- 5Department of Neurology, Nordsjællands Hospital, Hillerød, Denmark
- Jeppe Romme Christensen
- The Danish Multiple Sclerosis Registry, Copenhagen University Hospital, Rigshospitalet, Glostrup, Denmark
- Matthias Kant
- 6Department of Neurology, Hospital of Southern Jutland, University of Southern Denmark, Aabenraa, Denmark
- Morten Stilund
- 7Department of Neurology, Physiotherapy and Occupational Therapy, Gødstrup Hospital, Herning, Denmark
- Morten Stilund
- 8NIDO | Centre for Research and Education, Gødstrup Hospital, Herning, Denmark
- Henrik Mathiesen
- 9Department of Neurology, Copenhagen University Hospital Herlev and Gentofte, København, Denmark
- Jan Hillert
- Department of Clinical Neuroscience, Karolinska Institute, Stockholm, Sweden
- The Big MS Data Network: a collaboration of the Czech MS Registry, the Danish MS Registry, Italian MS Registry, Swedish MS Registry, MSBase Study Group, and OFSEP
- DOI
- https://doi.org/10.3389/fneur.2023.1274194
- Journal volume & issue
-
Vol. 14
Abstract
BackgroundTreatment switching is a common challenge and opportunity in real-world clinical practice. Increasing diversity in disease-modifying treatments (DMTs) has generated interest in the identification of reliable and robust predictors of treatment switching across different countries, DMTs, and time periods.ObjectiveThe objective of this retrospective, observational study was to identify independent predictors of treatment switching in a population of relapsing-remitting MS (RRMS) patients in the Big Multiple Sclerosis Data Network of national clinical registries, including the Italian MS registry, the OFSEP of France, the Danish MS registry, the Swedish national MS registry, and the international MSBase Registry.MethodsIn this cohort study, we merged information on 269,822 treatment episodes in 110,326 patients from 1997 to 2018 from five clinical registries. Patients were included in the final pooled analysis set if they had initiated at least one DMT during the relapsing-remitting MS (RRMS) stage. Patients not diagnosed with RRMS or RRMS patients not initiating DMT therapy during the RRMS phase were excluded from the analysis. The primary study outcome was treatment switching. A multilevel mixed-effects shared frailty time-to-event model was used to identify independent predictors of treatment switching. The contributing MS registry was included in the pooled analysis as a random effect.ResultsEvery one-point increase in the Expanded Disability Status Scale (EDSS) score at treatment start was associated with 1.08 times the rate of subsequent switching, adjusting for age, sex, and calendar year (adjusted hazard ratio [aHR] 1.08; 95% CI 1.07–1.08). Women were associated with 1.11 times the rate of switching relative to men (95% CI 1.08–1.14), whilst older age was also associated with an increased rate of treatment switching. DMTs started between 2007 and 2012 were associated with 2.48 times the rate of switching relative to DMTs that began between 1996 and 2006 (aHR 2.48; 95% CI 2.48–2.56). DMTs started from 2013 onwards were more likely to switch relative to the earlier treatment epoch (aHR 8.09; 95% CI 7.79–8.41; reference = 1996–2006).ConclusionSwitching between DMTs is associated with female sex, age, and disability at baseline and has increased in frequency considerably in recent years as more treatment options have become available. Consideration of a patient's individual risk and tolerance profile needs to be taken into account when selecting the most appropriate switch therapy from an expanding array of treatment choices.
Keywords
- multiple sclerosis
- disease modifying treatment (DMT)
- treatment switching
- disease registry
- real world evidence (RWE)