Brain-targeted ex vivo lentiviral gene therapy: Implications for MPS and beyond
Allison M. Bradbury
Affiliations
Allison M. Bradbury
Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children’s Hospital, Columbus, OH, USA; Department of Pediatrics, The Ohio State University, Columbus, OH, USA; Corresponding author: Allison M. Bradbury, Abigail Wexner Research Institute, Center for Gene Therapy, Columbus, OH, USA.