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Frontiers in Cellular Neuroscience
(May 2022)
Commentary: Current Status of Gene Therapy for Spinal Muscular Atrophy
Wilfried Rossoll,
Ravindra N. Singh
Affiliations
Wilfried Rossoll
Department of Neuroscience, Mayo Clinic, Jacksonville, FL, United States
Ravindra N. Singh
Department of Biomedical Sciences, Iowa State University, Ames, IA, United States
DOI
https://doi.org/10.3389/fncel.2022.916065
Journal volume & issue
Vol. 16
Abstract
Read online
No abstracts available.
Keywords
spinal muscular atrophy (SMA)
Survival Motor Neuron (SMN)
onasemnogene abeparvovec
Zolgensma
AVXS-101
gene therapy
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