Frontiers in Immunology (Jan 2024)
Case report: Cytopenias in VEXAS syndrome - a WHO 2022 based approach in a single-center cohort
- Elisa Diral,
- Corrado Campochiaro,
- Corrado Campochiaro,
- Alessandro Tomelleri,
- Alessandro Tomelleri,
- Gregorio M. Bergonzi,
- Gregorio M. Bergonzi,
- Umberto Pizzano,
- Umberto Pizzano,
- Maurilio Ponzoni,
- Maurilio Ponzoni,
- Lucia Bongiovanni,
- Lucia Bongiovanni,
- Paola Ronchi,
- Cristina Tresoldi,
- Silvia Rigamonti,
- Federico Scarfò,
- Federico Scarfò,
- Gloria M. Latino,
- Emma Rinaldi,
- Massimo Bernardi,
- Lorenzo Dagna,
- Lorenzo Dagna,
- Fabio Ciceri,
- Fabio Ciceri
Affiliations
- Elisa Diral
- Unit of Hematology, IRCCS San Raffaele Scientific Institute, Milan, Italy
- Corrado Campochiaro
- Unit of Immunology, Rheumatology, Allergy and Rare Diseases, IRCCS San Raffaele Scientific Institute, Milan, Italy
- Corrado Campochiaro
- School of Medicine, Vita-Salute San Raffaele University, Milan, Italy
- Alessandro Tomelleri
- Unit of Immunology, Rheumatology, Allergy and Rare Diseases, IRCCS San Raffaele Scientific Institute, Milan, Italy
- Alessandro Tomelleri
- School of Medicine, Vita-Salute San Raffaele University, Milan, Italy
- Gregorio M. Bergonzi
- Unit of Hematology, IRCCS San Raffaele Scientific Institute, Milan, Italy
- Gregorio M. Bergonzi
- School of Medicine, Vita-Salute San Raffaele University, Milan, Italy
- Umberto Pizzano
- Unit of Hematology, IRCCS San Raffaele Scientific Institute, Milan, Italy
- Umberto Pizzano
- School of Medicine, Vita-Salute San Raffaele University, Milan, Italy
- Maurilio Ponzoni
- School of Medicine, Vita-Salute San Raffaele University, Milan, Italy
- Maurilio Ponzoni
- Pathology Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy
- Lucia Bongiovanni
- School of Medicine, Vita-Salute San Raffaele University, Milan, Italy
- Lucia Bongiovanni
- Pathology Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy
- Paola Ronchi
- Unit of Immunohaematology and Transfusion Medicine, IRCCS San Raffaele Scientific Institute, Milan, Italy
- Cristina Tresoldi
- Unit of Immunohaematology and Transfusion Medicine, IRCCS San Raffaele Scientific Institute, Milan, Italy
- Silvia Rigamonti
- Unit of Immunohaematology and Transfusion Medicine, IRCCS San Raffaele Scientific Institute, Milan, Italy
- Federico Scarfò
- School of Medicine, Vita-Salute San Raffaele University, Milan, Italy
- Federico Scarfò
- Pathology Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy
- Gloria M. Latino
- School of Medicine, Vita-Salute San Raffaele University, Milan, Italy
- Emma Rinaldi
- School of Medicine, Vita-Salute San Raffaele University, Milan, Italy
- Massimo Bernardi
- Unit of Hematology, IRCCS San Raffaele Scientific Institute, Milan, Italy
- Lorenzo Dagna
- Unit of Immunology, Rheumatology, Allergy and Rare Diseases, IRCCS San Raffaele Scientific Institute, Milan, Italy
- Lorenzo Dagna
- School of Medicine, Vita-Salute San Raffaele University, Milan, Italy
- Fabio Ciceri
- Unit of Hematology, IRCCS San Raffaele Scientific Institute, Milan, Italy
- Fabio Ciceri
- School of Medicine, Vita-Salute San Raffaele University, Milan, Italy
- DOI
- https://doi.org/10.3389/fimmu.2024.1354130
- Journal volume & issue
-
Vol. 15
Abstract
VEXAS syndrome is an acquired autoinflammatory disease characterized in most cases by cytopenias and macrocytic anemia. Dyshematopoiesis is a frequent finding in chronic inflammatory conditions and therefore, cytopenias are not easily classified in VEXAS patients. Here we report a series of 7 patients affected by VEXAS associated cytopenias, treated at our center. The use of NGS, together with morphological assays, integrated with the WHO 2022 criteria, allowed to identify three subsets of VEXAS associated cytopenias: ICUS (idiopathic cytopenia of uncertain significance), CCUS (clonal cytopenia of uncertain significance) at high risk of clonal evolution, and MDS. This approach could help to better understand the nature of VEXAS associated cytopenias and to guide the use of specific targeted treatments in order to achieve long lasting responses.
Keywords
- myelodysplastic neoplasms (MDS)
- VEXAS syndrome
- next generating sequencing
- azacytidine
- ruxolitinib
- vacuoles