Molecular Therapy: Methods & Clinical Development (Jun 2024)
Strengthening health systems for access to gene therapy in rare genetic disorders
- Sonal Bhatia,
- Yann Le Cam,
- Juan Carrion,
- Lauren Diamond,
- Paul Fennessy,
- Safiyya Gassman,
- Felix Gutzwiller,
- Stephen Kagan,
- Diana Pankevich,
- Jennifer Young Maloney,
- Nitin Mahadev,
- Martin Schulz,
- Durhane Wong-Rieger,
- Paolo Morgese
Affiliations
- Sonal Bhatia
- Pfizer, Inc., New York, NY, USA
- Yann Le Cam
- EURORDIS, Paris, France
- Juan Carrion
- Aliber, Totana, Spain
- Lauren Diamond
- Pfizer, Inc., New York, NY, USA
- Paul Fennessy
- Paul Fennessy Advisory, Melbourne, VIC, Australia
- Safiyya Gassman
- Pfizer, Inc., New York, NY, USA
- Felix Gutzwiller
- University of Zurich, Zurich, Switzerland
- Stephen Kagan
- Pfizer, Inc., New York, NY, USA
- Diana Pankevich
- Pfizer, Inc., New York, NY, USA
- Jennifer Young Maloney
- Pfizer, Inc., New York, NY, USA
- Nitin Mahadev
- Pfizer, Inc., New York, NY, USA
- Martin Schulz
- Pfizer, Inc., New York, NY, USA; Corresponding author: Martin Schulz, Pfizer, Inc., New York, NY, USA.
- Durhane Wong-Rieger
- Canadian Organization for Rare Disorders, Toronto, ON, Canada
- Paolo Morgese
- Alliance for Regenerative Medicine, Brussels, Belgium
- Journal volume & issue
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Vol. 32,
no. 2
p. 101220